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Clinical outcomes in idursulfase-treated patients with mucopolysaccharidosis type II: 3-year data from the hunter outcome survey (HOS)

Creator: Muenzer, Joseph, Giugliani, Roberto, Scarpa, Maurizio, Tylki-SzymaƄska, Anna, Jego, Virginie, Beck, Michael

Abstract Background Mucopolysaccharidosis type II (MPS II; Hunter syndrome) is a rare, X-linked disorder caused by deficient activity of the enzyme iduronate-2-sulfatase (I2S). Treatment is available in the form of enzyme replacement therapy (ERT) (more)

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13023_2017_article_712.pdf

Collection: BioMed Central

Date Deposited: 2017-10-06

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Additional file 1: Table S1

Collection: BioMed Central

Date Deposited: 2017-10-06

Date Created: 2017-10-06

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Additional file 2: Table S2

Collection: BioMed Central

Date Deposited: 2017-10-06

Date Created: 2017-10-06

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Additional file 3: Table S3

Collection: BioMed Central

Date Deposited: 2017-10-06

Date Created: 2017-10-06

docx  (25.8 KB)